Laboratory evaluation of urea cycle disorders

J Pediatr. 2001 Jan;138(1 Suppl):S21-9. doi: 10.1067/mpd.2001.111833.

Abstract

The urea cycle disorders (UCDs) represent a group of inherited metabolic diseases with hyperammonemia as the primary laboratory abnormality. Affected individuals may become comatose or die if not treated rapidly. Diagnosis of a UCD requires a high index of suspicion and judicious use of the laboratory. It is important to rule out other conditions causing hyperammonemia that may require different treatment. The astute clinician may suspect a specific UCD in the appropriate clinical setting, but only laboratory results can confirm a specific diagnosis. The importance of the laboratory in helping the clinician to differentiate among various causes of hyperammonemia, in confirming a specific UCD, in carrier testing, and in prenatal diagnostic testing is highlighted in this review.

Publication types

  • Review

MeSH terms

  • Algorithms
  • Amino Acid Metabolism, Inborn Errors / diagnosis*
  • Citrulline / metabolism
  • DNA Mutational Analysis
  • Humans
  • Hyperammonemia / diagnosis*
  • Hyperammonemia / etiology
  • Orotic Acid / urine
  • Urea / metabolism*

Substances

  • Citrulline
  • Orotic Acid
  • Urea