3-Hydroxyisobutyric aciduria: phenotypic heterogeneity within a single family

Clin Dysmorphol. 2001 Jul;10(3):189-91. doi: 10.1097/00019605-200107000-00007.

Abstract

3-Hydroxyisobutyric aciduria is a rare biochemical finding associated with a variable clinical phenotype in the literature. We report two siblings excreting abnormal levels of this metabolite from a consanguineous family who manifested distinct phenotypic variation. We speculate as to whether this biochemical anomaly may simply be an incidental finding and suggest that pre-natal counselling on the basis of metabolite identification may be unwarranted.

Publication types

  • Case Reports

MeSH terms

  • Child
  • Family Health
  • Female
  • Genetic Heterogeneity
  • Humans
  • Hydroxybutyrates / urine*
  • Male
  • Metabolism, Inborn Errors / genetics*
  • Metabolism, Inborn Errors / urine*
  • Microcephaly / genetics*
  • Microcephaly / urine*
  • Phenotype

Substances

  • Hydroxybutyrates
  • 3-hydroxyisobutyric acid