Prenatal diagnosis of Pompe disease: enzyme assay or molecular testing?

Indian Pediatr. 2011 Nov 11;48(11):901-2. doi: 10.1007/s13312-011-0130-x.

Abstract

We report two cases which illustrate that enzyme assay results alone, may at times be equivocal and inconclusive in the prenatal diagnosis of storage disorders like Pompe disease and therefore, if the probands mutation is known, targeted mutation analysis of fetal DNA is the most reliable method for fetal evaluation.

Publication types

  • Case Reports

MeSH terms

  • DNA Mutational Analysis
  • Female
  • Genetic Testing
  • Glycogen Storage Disease Type II / diagnosis*
  • Glycogen Storage Disease Type II / genetics*
  • Humans
  • Pregnancy
  • Prenatal Diagnosis / methods*