Angelman Syndrome Due to UBE3A Gene Mutation

Indian J Pediatr. 2018 May;85(5):390-391. doi: 10.1007/s12098-017-2559-y. Epub 2017 Dec 18.

Abstract

A 12-y-old boy presented with developmental delay, autism, epilepsy, limb tremors and behavioral problems which posed a diagnostic challenge. Though his clinical profile and electroencephalogram were suggestive of Angelman syndrome, initial genetic tests were unyielding. Exome sequencing revealed a previously unreported mutation of Ubiquitin Protein Ligase E3A (UBE3A) gene, confirming the diagnosis of Angelman syndrome. The case is aimed to sensitize pediatricians about Angelman syndrome and to highlight the role of sequential investigations in establishing the diagnosis.

Keywords: Angelman syndrome; Happy Puppet syndrome; UBE3A; Ubiquitin Protein Ligase E3A.

Publication types

  • Case Reports

MeSH terms

  • Angelman Syndrome / diagnosis
  • Angelman Syndrome / genetics*
  • Child
  • Chromosomes, Human, Pair 15
  • Exons
  • Genetic Testing
  • Humans
  • Male
  • Mutation*
  • Ubiquitin-Protein Ligases / genetics*

Substances

  • UBE3A protein, human
  • Ubiquitin-Protein Ligases