Frataxin Restoration in the Nervous System: Possibilities for Gene Therapy

Mol Ther. 2018 Aug 1;26(8):1880-1882. doi: 10.1016/j.ymthe.2018.06.006. Epub 2018 Jun 30.

Authors

David R Lynch¹, Elizabeth Kichula², Hong Lin²

Affiliations

¹ Division of Neurology, Children's Hospital of Philadelphia, 502 Abramson Research Center, 3615 Civic Center Boulevard, Philadelphia, PA 19104, USA. Electronic address: lynchd@mail.med.upenn.edu.
² Division of Neurology, Children's Hospital of Philadelphia, 502 Abramson Research Center, 3615 Civic Center Boulevard, Philadelphia, PA 19104, USA.

No abstract available

Publication types

Research Support, N.I.H., Extramural
Research Support, Non-U.S. Gov't
Research Support, U.S. Gov't, P.H.S.
Comment

MeSH terms

Ataxia
Frataxin
Friedreich Ataxia*
Genetic Therapy
Humans
Iron-Binding Proteins / genetics

Substances

Iron-Binding Proteins