Clinical trial strategies for rare neurodevelopmental disorders: challenges and opportunities

Nat Rev Drug Discov. 2021 Sep;20(9):653-654. doi: 10.1038/d41573-021-00085-9.
No abstract available

MeSH terms

  • Clinical Trials as Topic / methods*
  • Humans
  • Neurodevelopmental Disorders / genetics
  • Neurodevelopmental Disorders / physiopathology
  • Neurodevelopmental Disorders / therapy*
  • Rare Diseases / genetics
  • Rare Diseases / physiopathology
  • Rare Diseases / therapy*
  • Research Design