CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia

N Engl J Med. 2021 Jun 10;384(23):e91. doi: 10.1056/NEJMc2103481.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Anemia, Sickle Cell* / genetics
  • Anemia, Sickle Cell* / therapy
  • CRISPR-Cas Systems
  • Clustered Regularly Interspaced Short Palindromic Repeats
  • Gene Editing
  • Humans
  • beta-Thalassemia* / genetics
  • beta-Thalassemia* / therapy