Ichthyosis, petechiae, and arthrogryposis in a neonate

Pediatr Dermatol. 2023 Mar;40(2):352-354. doi: 10.1111/pde.15169. Epub 2022 Nov 5.

Abstract

Gaucher disease is a rare lysosomal storage disorder caused by a deficiency in glucocerebrosidase. This enzyme deficiency leads to the accumulation of toxic metabolites in various organs. Multiple subtypes of this disease have been described; however, the perinatal-lethal form is extremely rare and challenging to diagnose. We present a case of a newborn girl with ichthyosis, petechiae, and arthrogryposis, later found to be homozygous for a pathogenic variant of the glucocerebrosidase gene. This case highlights the potential role of dermatologists in the recognition of this rare disease.

Keywords: Gaucher disease; ichthyosis; perinatal-lethal.

Publication types

  • Case Reports

MeSH terms

  • Arthrogryposis* / complications
  • Arthrogryposis* / diagnosis
  • Arthrogryposis* / genetics
  • Female
  • Gaucher Disease* / genetics
  • Gaucher Disease* / pathology
  • Glucosylceramidase / genetics
  • Glucosylceramidase / metabolism
  • Humans
  • Ichthyosis* / genetics
  • Ichthyosis, Lamellar* / complications
  • Infant, Newborn
  • Pregnancy
  • Purpura*

Substances

  • Glucosylceramidase