Gene therapy offers promise, but timing is crucial for SMA treatment

Eur J Paediatr Neurol. 2024 Jul:51:A2-A3. doi: 10.1016/j.ejpn.2024.07.005. Epub 2024 Jul 8.
No abstract available

Publication types

  • Editorial

MeSH terms

  • Genetic Therapy* / methods
  • Genetic Therapy* / trends
  • Humans
  • Muscular Atrophy, Spinal / genetics
  • Muscular Atrophy, Spinal / therapy