Small-molecule modulators of B56-PP2A restore 4E-BP function to suppress eIF4E-dependent translation in cancer cells

J Clin Invest. 2025 Jan 27;135(4):e176093. doi: 10.1172/JCI176093.

Abstract

Dysregulated eIF4E-dependent translation is a central driver of tumorigenesis and therapy resistance. eIF4E-binding proteins (4E-BP1/2/3) are major negative regulators of eIF4E-dependent translation that are inactivated in tumors through inhibitory phosphorylation or downregulation. Previous studies have linked PP2A phosphatase(s) to activation of 4E-BP1. Here, we leveraged biased small-molecule activators of PP2A (SMAPs) to explore the role of B56-PP2A(s) in 4E-BP regulation and the potential of B56-PP2A activation for restoring translational control in tumors. SMAP treatment promoted PP2A-dependent hypophosphorylation of 4E-BP1/2, supporting a role for B56-PP2As (e.g., B56α-PP2A) as 4E-BP phosphatases. Unexpectedly, SMAPs induced transcriptional upregulation of 4E-BP1 through a B56-PP2A→TFE3/TFEB→ATF4 axis. Cap-binding and coimmunoprecipitation assays showed that B56-PP2A(s) activation blocks assembly of the eIF4F translation initiation complex, and cap-dependent translation assays confirmed the translation-inhibitory effects of SMAPs. Thus, B56-PP2A(s) orchestrate a translation-repressive program involving transcriptional induction and activation of 4E-BP1. Notably, SMAPs promoted 4E-BP1-dependent apoptosis in tumor cells and potentiated 4E-BP1 function in the presence of ERK or mTOR inhibitors, agents that rely on inhibition of eIF4E-dependent translation for antitumor activity. These findings, combined with the ability of SMAPs to regulate 4E-BP1 in vivo, highlight the potential of PP2A activators for cancer therapy and overcoming therapy resistance.

Keywords: Cell biology; Oncology; Phosphoprotein phosphatases; Signal transduction; Translation.

MeSH terms

  • Activating Transcription Factor 4 / genetics
  • Activating Transcription Factor 4 / metabolism
  • Adaptor Proteins, Signal Transducing* / genetics
  • Adaptor Proteins, Signal Transducing* / metabolism
  • Animals
  • Cell Cycle Proteins
  • Cell Line, Tumor
  • Eukaryotic Initiation Factor-4E* / genetics
  • Eukaryotic Initiation Factor-4E* / metabolism
  • Eukaryotic Initiation Factors* / genetics
  • Eukaryotic Initiation Factors* / metabolism
  • Humans
  • Mice
  • Neoplasm Proteins* / genetics
  • Neoplasm Proteins* / metabolism
  • Neoplasms* / drug therapy
  • Neoplasms* / genetics
  • Neoplasms* / metabolism
  • Neoplasms* / pathology
  • Phosphoproteins* / genetics
  • Phosphoproteins* / metabolism
  • Phosphorylation / drug effects
  • Protein Biosynthesis* / drug effects
  • Protein Phosphatase 2* / genetics
  • Protein Phosphatase 2* / metabolism
  • Small Molecule Libraries* / pharmacology

Substances

  • Protein Phosphatase 2
  • EIF4EBP1 protein, human
  • Adaptor Proteins, Signal Transducing
  • Cell Cycle Proteins
  • Eukaryotic Initiation Factor-4E
  • EIF4E protein, human
  • Phosphoproteins
  • EIF4EBP2 protein, human
  • Eukaryotic Initiation Factors
  • Activating Transcription Factor 4
  • Small Molecule Libraries
  • ATF4 protein, human
  • Neoplasm Proteins