The association of lipids and novel non-statin lipid-lowering drug target with osteoporosis: evidence from genetic correlations and Mendelian randomization

BMC Musculoskelet Disord. 2025 Feb 1;26(1):107. doi: 10.1186/s12891-024-08160-z.

Abstract

Background: It remains controversial whether lipids affect osteoporosis (OP) or bone mineral density (BMD), and causality has not been established. This study aimed to investigate the genetic associations between lipids, novel non-statin lipid-lowering drug target genes, and OP and BMD.

Methods: Mendelian randomization (MR) method was used to explore the genetic associations between 179 lipid species and OP, BMD. Drug-target MR analysis was used to explore the causal associations between angiopoietin-like protein 3 (ANGPTL3) and apolipoprotein C3 (APOC3) inhibitors on BMD.

Results: The IVW results with Bonferroni correction indicated that triglyceride (TG) (51:3) (OR = 1.0029; 95% CI: 1.0014-1.0045; P = 0.0002) and TG (56:6) (OR = 1.0021; 95% CI: 1.0008-1.0033; P = 0.0011) were associated with an increased risk of OP; TG (51:2) (OR = 0.9543; 95% CI: 0.9148-0.9954; P = 0.0298) was associated with decreased BMD; and ANGPTL3 inhibitor (OR = 1.1342; 95% CI: 1.0393-1.2290; P = 0.0093) and APOC3 inhibitor (OR = 1.0506; 95% CI: 1.0155-1.0857; P = 0.0058) was associated with increased BMD.

Conclusions: MR analysis indicated causal associations between genetically predicted TGs and OP and BMD. Drug-target MR analysis showed that ANGPTL3 and APOC3 have the potential to serve as novel non-statin lipid-lowering drug targets to treat or prevent OP.

Keywords: ANGPTL3; APOC3; Bone mineral density; Drug target Mendelian randomization; Lipids; Osteoporosis.

MeSH terms

  • Angiopoietin-Like Protein 3 / genetics
  • Angiopoietin-like Proteins / genetics
  • Apolipoprotein C-III* / antagonists & inhibitors
  • Apolipoprotein C-III* / genetics
  • Bone Density* / drug effects
  • Bone Density* / genetics
  • Female
  • Genetic Association Studies / methods
  • Humans
  • Hypolipidemic Agents* / therapeutic use
  • Lipids* / blood
  • Mendelian Randomization Analysis / methods
  • Osteoporosis* / blood
  • Osteoporosis* / drug therapy
  • Osteoporosis* / epidemiology
  • Osteoporosis* / genetics
  • Polymorphism, Single Nucleotide
  • Triglycerides / blood

Substances

  • Angiopoietin-Like Protein 3
  • ANGPTL3 protein, human
  • Hypolipidemic Agents
  • Apolipoprotein C-III
  • Triglycerides
  • Lipids
  • APOC3 protein, human
  • Angiopoietin-like Proteins