Targeted inhibition of pathobiont virulence factor mitigates alcohol-associated liver disease

Cell Host Microbe. 2025 Jun 11;33(6):957-972.e6. doi: 10.1016/j.chom.2025.05.003. Epub 2025 May 28.

Abstract

Alcohol-associated liver disease poses a global health burden with high mortality. Imbalances in the gut microbiota are important for disease progression. Using metagenomic sequencing of fecal samples from a multicenter, international cohort of patients with alcohol-associated hepatitis, we found that the presence of virulence factor KpsM, encoded in the genome of Escherichia coli (E. coli), correlated with patient mortality. Functional studies using gnotobiotic mouse models and genetic manipulation of bacteria demonstrated that kpsM-positive E. coli exacerbate ethanol-induced liver disease. The kpsM gene mediates the translocation of capsular polysaccharides to the cell surface. This enables kpsM-positive E. coli to evade phagocytosis by the scavenger receptor Marco on Kupffer cells in the liver, leading to bacterial spread. Importantly, inhibiting kpsM-dependent capsules with the small molecule 2-(4-phenylphenyl)benzo[g]quinoline-4-carboxylic acid (C7) attenuated ethanol-induced liver disease in mice. We show that precision targeting of the virulence factor KpsM is a promising approach to improve outcomes of patients with alcohol-associated hepatitis.

Keywords: alcoholic liver disease; gut-liver axis; metagenomics; microbiome; microbiota; virulence factor.

MeSH terms

  • Animals
  • Bacterial Capsules / metabolism
  • Disease Models, Animal
  • Escherichia coli Infections / microbiology
  • Escherichia coli Proteins* / antagonists & inhibitors
  • Escherichia coli Proteins* / genetics
  • Escherichia coli Proteins* / metabolism
  • Escherichia coli* / drug effects
  • Escherichia coli* / genetics
  • Escherichia coli* / metabolism
  • Escherichia coli* / pathogenicity
  • Ethanol
  • Feces / microbiology
  • Female
  • Gastrointestinal Microbiome
  • Germ-Free Life
  • Hepatitis, Alcoholic / microbiology
  • Humans
  • Kupffer Cells / metabolism
  • Kupffer Cells / microbiology
  • Liver / microbiology
  • Liver / pathology
  • Liver Diseases, Alcoholic* / drug therapy
  • Liver Diseases, Alcoholic* / microbiology
  • Male
  • Mice
  • Mice, Inbred C57BL
  • Virulence Factors* / antagonists & inhibitors
  • Virulence Factors* / genetics
  • Virulence Factors* / metabolism

Substances

  • Virulence Factors
  • Escherichia coli Proteins
  • Ethanol