In utero genetic therapy: Treatment of early onset neurological disorders before they start

Affiliations

• ¹ Department of Surgery, University of California, San Francisco, San Francisco, CA 94143, USA; UCSF Center for Maternal-Fetal Precision Medicine, San Francisco, CA 94158, USA; The Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, University of California, San Francisco, San Francisco, CA 94143, USA.
• ² Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, MD 21205, USA; Department of Neuroscience, Johns Hopkins University School of Medicine, Baltimore, MD 21205, USA.
• ³ Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, MD 21205, USA; Department of Neuroscience, Johns Hopkins University School of Medicine, Baltimore, MD 21205, USA; Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, MD 21205, USA. Electronic address: csumner1@jhmi.edu.