Insights from ADPedKD, ERKReg and RaDaR registries provide a multi-national perspective on the presentation of childhood autosomal dominant polycystic kidney disease in high- and middle-income countries.
Gimpel C, Fieuws S, Hofstetter J, Pitcher D, Vanmeerbeek L, Haeberle S, Dachy A, Massella L, Seeman T, Ranchin B, Allard L, Bacchetta J, Bayrakci US, Becherucci F, Perez-Beltran V, Besouw M, Bialkevich H, Boyer O, Canpolat N, Chauveau D, Çiçek N, Conlon PJ, Devuyst O, Dossier C, Fila M, Flögelová H, Godron-Dubrasquet A, Gokce I, Nguyen-Tang EG, González-Rodríguez JD, Guffens A, Grandaliano G, Heidet L, Jankauskiene A, Levart TK, Knebelmann B, König JC, La Scola C, Leone VF, Leroy V, Litwin M, Lucchetti L, Lungu AC, Marzuillo P, Mastrangelo A, Miklaszewska M, Montini G, Nobili F, Obrycki L, Papizh S, Paripović A, Paripović D, Peruzzi L, Raes A, Saygili S, Spasojević B, Simon T, Szczepańska M, Trepiccione F, Varda NM, Westland R, Yüksel S, Zaluska-Lesniewska I, Tenebaum J, Mustafa R, Mallett AJ, Guay-Woodford LM, Gale DP, Böckenhauer D, Liebau MC, Schaefer F, Mekahli D; RaDaR ADPKD Rare Disease Group; ERKReg Collaborators; ADPedKD Collaborators.
Gimpel C, et al.
Kidney Int. 2025 Jul;108(1):105-118. doi: 10.1016/j.kint.2025.02.026. Epub 2025 Mar 21.
Kidney Int. 2025.
PMID: 40122340
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