Opinion of the Italian Association of Myology on Ataluren for the Treatment of Nonsense Mutation Duchenne Muscular Dystrophy.
Bello L, Riguzzi P, Albamonte E, Astrea G, Battini R, Barp A, Berardinelli AL, Bertini ES, Brolatti N, Bruno C, Corti S, D'Amico A, D'Angelo MG, Dallavalle G, Liguori R, Maggi L, Magri F, Mancuso M, Masson R, Mercuri E, Minetti C, Messina S, Mongini T, Musumeci O, Nigro V, Pane M, Panicucci C, Pedemonte M, Pini A, Politano L, Previtali S, Ricci F, Ricci G, Ruggiero L, Sansone V, Siciliano G, Trabacca A, Trucco F, Velardo D, Pegoraro E, Comi GP.
Bello L, et al. Among authors: minetti c.
Drugs R D. 2025 Jun;25(2):99-106. doi: 10.1007/s40268-025-00512-x. Epub 2025 May 28.
Drugs R D. 2025.
PMID: 40434600
Free PMC article.
Review.