Longitudinal Assessment of 4-Year HFMSE Changes in SMA II and III Patients Treated With Nusinersen.
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Coratti G, et al. Among authors: hirano m.
Eur J Neurol. 2025 Jul;32(7):e70268. doi: 10.1111/ene.70268.
Eur J Neurol. 2025.
PMID: 40576143
Free PMC article.