A TMPRSS6-inhibiting mAb improves disease in a β-thalassemia mouse model and reduces iron in healthy humans.
Lob HE, Singh N, Mohammadi K, Ivanova L, Crowell B, Kim HJ, Kravets L, Das NM, Ray Y, Kim JH, Rottey S, Labriola-Tompkins E, Hassan HE, Farrelly L, Chin HF, Preda M, Spencer Noakes L, Saotome K, Franklin M, Retter MW, Karayusuf E, Flanagan JJ, Olson W, Nannuru KC, Idone V, Burczynski ME, Harari OA, Perlee L, Van Lancker G, Murphy AJ, Economides AN, Hatsell SJ.
Lob HE, et al. Among authors: harari oa.
JCI Insight. 2025 Jun 23;10(12):e191813. doi: 10.1172/jci.insight.191813. eCollection 2025 Jun 23.
JCI Insight. 2025.
PMID: 40548380
Free article.
Clinical Trial.